Access to gene therapy for rare dieseases when commercialization is not fit for purpose
March 1, 2023 2:29 pmFox T, Bueren J, Candotti F, Fischer A, Aiuti A, Lankester A; AGORA Initiative; Booth C. Access to gene therapy for rare diseases when commercialization is not fit for purpose. Nat Med. 2023 Feb 13. doi: 10.1038/s41591-023-02208-8.
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This post was written by Heike Ufheil
